Search for Clinical Trial Results
Mucopolysaccharidosis II - 50 Studies Found
Status | Study |
Active, not recruiting |
Study Name: A Open Label Study in Previously Studied, SBC-103 Treatment Naïve MPS IIIB Subjects to Investigate the Safety, Pharmacokinetics, and Pharmacodynamics/Efficacy of SBC-103 Administered Intravenously Condition:
Date: 2015-10-21 Interventions: Drug: SBC-103 |
Completed |
Study Name: Randomized, Controlled, Open-label, Multicenter, Safety and Efficacy Study of rhHNS Administration Via an IDDD in Pediatric Patients With Early Stage MPS IIIA Disease Condition: Sanfilippo Syndrome Date: 2014-02-10 Interventions: Drug: Recombinant human heparan N-sulfatase [rhHNS] Recombinant human heparan N-sulfatase [rhHNS] |
Completed |
Study Name: A Retrospective Chart Review of Deceased Patients With Mucopolysaccharidosis Type IIIB Condition: MPS IIIB (Sanfilippo Syndrome) Date: 2014-11-03 |
Active, not recruiting |
Study Name: Long-term Follow-up of Sanfilippo Type A Patients Treated by Intracerebral SAF-301 Gene Therapy Condition:
|
Completed |
Study Name: Intracerebral Gene Therapy for Sanfilippo Type A Syndrome Condition:
|
Recruiting |
Study Name: Biomarker for Sanfilippo Disease Condition:
|
Enrolling by invitation |
Study Name: An Extension Study to Determine Safety and Efficacy for Pediatric Patients With MPS Type IIIA Disease Who Participated in Study HGT-SAN-093. Condition:
Date: 2015-01-21 Interventions: Drug: HGT-1410 HGT-1410 administered according to Patient Group assignment. |
Recruiting |
Study Name: A Treatment Study of Mucopolysaccharidosis Type IIIB Condition:
Date: 2016-02-27 Interventions: Drug: BMN 250 Chimeric fusion of recombinant human alpha-N-acetylglucosaminidase and truncated human ins |
Completed |
Study Name: Neurobehavioral Phenotypes in MPS III Condition:
|